World Orphan Drug Congress Europe 2026
The World Orphan Drug Congress Europe returns to Amsterdam from 26–28 October 2026, bringing together the global rare disease and orphan drug community for three days of collaboration, innovation and […]
Conference
RAREsummit25: CamRARE at 10 – Connecting Moments
2025 marks a special milestone — CamRARE’s 10th anniversary. A decade of progress. A future of possibilities. Over the past decade, we have championed collaboration, amplified patient voices, and driven […]
‘First Do No Harm’: Expert Reflections on a Rare Bone Disease’
JOIN US AT THE HUNTERIAN MUSEUM! Join Medics4RareDiseases and FOP Friends for a unique reception, at the prestigious Hunterian Museum, at the Royal College of Surgeons of England on 13th […]
Annual Lafora Disease Science Symposium
Lafora disease researchers and clinicians at Instituto delle Scienze Neurologiche di Bologna (ISNB) IRCCS will host the 8th Annual Lafora Disease Science Symposium in Bologna, Italy from October 9-10, 2023. Chelsea’s Hope […]
Journal Club: On the 12th Day of Christmas, a statistician said to me…
The month’s leading up to Christmas are a magical time for medical research. The impending holiday season creates a dynamic upsurge in productivity, with researchers finding time to finish off […]
The Importance of Centering the Patient by Nadine Jefferies
How can pharmaceutical companies ensure that patients are actively involved at every stage ofdrug development? Last week I attended the Patient Centricity & Engagement conference in London to find out […]
Pint of Science Festival
Our Rare Mind and Rare Body events for the International Pint of Science Festival are now live! Join us for engaging research talks and interactive activities in the pub with […]
Patient Centricity and Engagement
29 Industry Leaders From Pharma, Advocacy Groups & Patients Themselves Share Their Latest Insights Into Driving Forward Patient Engagement Through Embedded Partnerships In Just One Day! Advanced, High-Impact, Value-Adding Strategies For […]
LinkAGE Webinar: Repurposing drugs for rare disease
Following on from the first three Genomics Education Programme webinars in the LinkAGE series, the next talk followed by a live Q&A will be broadcast on Thursday 20 April at […]
Advanced Therapies Conference at the ExCel in London by Nadine Jefferies
Hello, Nadine here, I’m back again! This time it’s to talk about rare disease policy. This month I attended Europe’s largest cell and gene therapy exhibition at the ExCel Centre.Among […]